Original Song Written to Help Raise Money for GM1 Research. Gangliosidosis is a lipid storage disorder caused by the accumulation of lipids known as gangliosides. There are two distinct genetic causes of the disease. Both are autosomal recessive and affect males and females equally. On Friday, March 20, 2015. JAN 2016 - Enzyme replacement for GM1-gangliosidosis.

Non-profit foundation dedicated to find a treatment and cure for GM1 Gangliosidosis. Non-profit foundation dedicated to find a treatment and cure of GM1 Gangliosidosis. GM1 Gangliosidosis is a rare disease. It is an autosomal recessive lysosomal storage disease. This category of diseases includes more than 50 conditions. GM1 Gangliosidosis robs children of nearly every skill and bodily function required to live. Human Trials are Within Reach Donate Now.

Our beautiful daughter, Jordyn, has been diagnosed with a rare, degenerative and life threatening lysosomal storage disease called G. Gangliosidosis is a metabolic disease that occurs when the same defective enzyme gene is inherited from each parent. It is estimated to occur 1 in every 100,000 to 200,000 live births. Our cells contain something called lysosomes. Gangliosidosis is one such disease. What Research is Being Done? Although enzyme replacement th.